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CF10 – Cystinosis About Cystinosis

About us

We are a pharmaceutical company spun out of the University of Sunderland, committed to the development of effective medicinal treatments in therapeutic areas where there is unmet clinical need.

About Cystinosis

Core values

We are driven by a fresh perspective to pair technical expertise with compassion to build an organisation that supports our communities. We are dedicated to creating profound positive societal benefit to patients and the healthcare community, engaging in drug discovery and development to bring to market products that:

Target real unmet clinical need

Are cost effective

Offer greater prescriber and patient choice in circumstances where there are: 

Limited treatment options available

Where treatment options are restricted on the basis of cost


10 Years of age

Approximate age at which kidney failure would occur if the disease was left untreated

About Projects

Active Projects

Sundara Pharma is developing a novel treatment for Nephropathic Cystinosis and a pipeline of novel compounds as sustainable treatments for diseases in a variety of therapeutic areas.

DISCOVER

About Cystinosis

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DISCOVER

CF10 – Cystinosis

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Cystinosis in numbers

60%

Expected rate of growth in untreated children with cystinosis1

22.7%

Of Cystinosis patients were found to be fully compliant with Cystagon therapy22

5%

Of all childhood cases of kidney failure are due to Cystinosis11

CF10 – CystinosisAbout Cystinosis

1 National Organisation for Rare Disorders 2021, Cystinosis, National Organisation for Rare Disorders, viewed 13th January 2021, https://rarediseases.org/rare-diseases/cystinosis/
2 Levtchenko et al. Strict Cysteamine dose regimen is required to prevent nocturnal cystine accumulation in cystinosis. Pediatric Nephrology. 2006;21:110.

Our Team

We have a skilled, qualified team and experienced team in drug discovery, development, regulatory affairs, IP protection and commercialisation.

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Revolutionised quality of life for patients

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